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List of All Articles with Tag 'duchenne'

US FDA approves Sarepta's gene therapy for rare muscular dystrophy in some kids
US FDA approves Sarepta's gene therapy for rare muscular dystrophy in some kids
By Leroy Leo and Aditya Samal (Reuters) -The U.S. Food and Drug Administration on Thursday granted accelerated approval to Sarepta
2023-06-23 02:59
Families facing rare muscle disease are pushing for an experimental gene therapy, but the FDA is skeptical
Families facing rare muscle disease are pushing for an experimental gene therapy, but the FDA is skeptical
SRP-9001, an experimental gene therapy that aims to slow or stop the progression of Duchenne muscular dystrophy, is being considered for accelerated approval by the FDA.
2023-05-12 22:27